Onasemnogene abeparvovec

Definition: Onasemnogene abeparvovec, sold under the brand name Zolgensma, is a gene therapy used to treat spinal muscular atrophy (SMA), a disease causing muscle function loss in children. It involves a one-time infusion of the medication into a vein. It works by providing a new copy of the SMN gene that produces the SMN protein. source: Wikipedia

ID

788110002

ID date

7 Jan 2022

Previous ID

39378211000001105

Name

Onasemnogene abeparvovec