Atidarsagene autotemcel

Definition: Atidarsagene autotemcel, sold under the brand name Libmeldy among others, is a gene therapy treatment for metachromatic leukodystrophy developed by Orchard Therapeutics. It contains an autologous CD34⁺ cell enriched population that contains haematopoietic stem and progenitor cells transduced using a lentiviral vector encoding the human arylsulfatase A (ARSA) gene. The most common side effects include fever and low white blood cell count, mouth sores, respiratory infections, rash, medical line in... source: Wikipedia

ID

1363393003

ID date

6 Oct 2025

Previous ID

40518611000001102

Name

Atidarsagene autotemcel