Alglucosidase alfa

Definition: Alglucosidase alfa, sold under the brand name Myozyme among others, is an enzyme replacement therapy (ERT) orphan drug for treatment of Pompe disease (Glycogen storage disease type II), a rare lysosomal storage disorder (LSD). Chemically, the drug is an analog of the enzyme that is deficient in patients affected by Pompe disease, alpha-glucosidase. source: Wikipedia

ID

703393008

ID date

20 Apr 2018

Previous ID

10901411000001100

Name

Alglucosidase alfa